Accelerating Hope: The Pathway for Cures

Episode 69 • Mar 28, 2023 • 23 min

Accelerating Hope: The Pathway for Cures

Episode Topic:

When people were dying from AIDS in the 1980s and 90s, Congress found a way to expedite the drug approval process and saved countless lives. Established in 1992, the Accelerated Approval Program allows the FDA to speed approval of drugs for patients with serious and life-threatening conditions. In this episode we talk with the father of children with a rare disease, a company CEO working to treat rare diseases and two policy experts on Accelerated Approval.

Episode Guests

John Crowley

Executive Chairman, Amicus Therapeutics

Emil D. Kakkis

CEO and President, Ultragenyx

Cartier Esham

Senior Advisor, BIO

Duane Schulthess

CEO, Vital Transformation

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