Day 1

9:30 AM

BioSafe Annual Meeting Opening Remarks

Christina de Zafra (Seagen), BioSafe Vice Chair

9:40 AM

BioSafe Overview

Jacintha Shenton (Amgen), BioSafe Chair

Oct 4
Session 1: Non-Human Primate Availability and Use
October 4, 2022 ・ 10:00AM - 2:35PM ET
 
Session Chairs: Lucinda Weir (GSK) and Jennifer Brown (MacroGenics)
 

10:00 AM

Session Overview

Session Chairs

10:30 AM

Proceedings from the 2021 FDA/BioSafe/DruSafe Annual Meeting

Jorg Blumel (Genentech)

11:05 AM

Update on NHP Availability: CRO Perspective

Candace Heining (Charles River Laboratories)

11:40 AM

Reuse of Protein Non-Naïve Monkeys in Pharmaceutical Research and Development

Chuck Mattis (Abbvie)

12:15 PM

Break

12:45 PM

BioSafe White Paper - Non-Human Primates in the PKPD Evaluation of Biologics: Needs and Options to Reduce, Refine and Replace

Karelle Menochet (UCB), Hongbin Yu (Boehringer Ingelheim)

1:20 PM

Alternatives to Supporting Human Dose and Drug Exposure Predictions with Cynomolgus Monkey PKPD Studies

Dan Rycroft (GSK), James Yates (GSK)

1:55 PM

Further Opportunities for NHP Use in Toxicology Studies with mAbs: Update from an MEB/Industry/NC3Rs Project Sponsored by EPAA

David Clarke (Eli Lilly & Co.)

2:30 PM

Session Closing Remarks

Lucinda Weir (GSK), Jennifer Brown (MacroGenics)

Afternoon Networking Session at 2:35PM ET
Day 2
Morning Networking Session @ 9:30AM ET
Oct 5
Session 2: RNA and Oligonucleotide Therapeutics
October 5, 2022 ・ 10:00AM - 1:55PM ET
 
Session Chairs: Katie Heinz-Taheny (Eli Lilly & Co.) and Kevin Donnelly (Eli Lilly & Co.)
 

10:00 AM

Session Overview

Chairs

10:05 AM

Concepts of Nucleic Acid Pharmaceuticals

Rebecca Kohnken (Abbvie)

10:50 AM

PK/ADME of Nucleic Acid Pharmaceuticals

Chris Wiethoff (Eli Lilly & Co.)

11:20 AM

Break

11:35 AM

Safety Assessment of siRNA and ASO Pharmaceuticals

Jen Sisler (Eli Lilly & Co.)

12:00 PM

Case Study: siRNA DART Strategies

Mark Carfagna (Eli Lilly & Co.)

12:20 PM

Nucleic Acid-Based Vaccines

Cindy Rohde (Pfizer)

12:50 PM

MRI Investigation of Total and Local CSF Volumes in Juvenile and Mature NHPs for the Preclinical Safety Assessment of ASOs

Lutz Mueller (Roche)

1:20 PM

Panel Discussion/Q&A

Afternoon Networking Session @ 1:55PM ET
Day 3
Oct 6
Session 3: Novel Approaches in Biopharmaceutical Development
October 6, 2022 ・ 9:00AM - 12:25PM ET
 
Session Chairs: Ulrike Hopfer (Roche) and Chandrashekhar Korgaonkar (Regeneron)
 

9:00 AM

Session Overview

Chairs

9:05 AM

EIH Approach and Discussion with Health Authorities for an MHC Targeting Bispecific Antibody for a Non-Oncology Indication

Hisashi Ikegami (Chugai Pharmaceuticals)

9:35 AM

Applications for a Virus-Like Particle and its TLR9 Agonist Cargo

Meredith Crosby (Regeneron)

10:05 AM

Bringing T Cell Receptor Therapeutics to Cancer Patients with a Patient-Centric in Vitro / ex Vivo Only Translational Approach

Estelle Marrer-Berger (Roche)

10:35 AM

Break

10:50 AM

Artificial Intelligence in Toxicology/Pathology

Andy Vo (Abbvie), Bhupinder Bawa (Abbvie)

11:40 PM

Preclinical Development of a Novel, Half-Life Extended Enzyme Biologic: Immunogenicity Considerations

Hema Gursahani (Jazz Pharmaceuticals)

12:05 PM

Panel Discussion/Q&A

12:25 PM

Break

Oct 6
Session 4: Biologics, Part I
October 6, 2022 ・ 12:40PM - 3:05PM ET
 
Session Chairs: Katy Fraser (Takeda), Maggie Willer (Takeda), Smita Salian-Mehta (Gilead)
 

12:40 PM

Session Overview

Chairs

12:45 PM

FIH Dose Strategies: Case Study Perspectives for Immunomodulators

Ryan Polli (Novartis)

1:15 PM

Novel FIH Approaches and Considerations for Biologics

Amy Sharma (Pfizer)

1:45 PM

Adventures in “IND-ing” with Immunostimulatory Biologics

Carole Harbison (Takeda)

2:15 PM

First-in-Human Dosing for an Immuno Modality in a Non-Oncology Indication: A Case Study

Rutwij Dave (Gilead)

2:45 PM

Panel Discussion/Q&A

Day 4
Morning Networking Session @ 9:30AM ET
Oct 11
Session 5: Fluid-Based Neurobiomarkers
October 11, 2022 ・ 10:00AM - 12:35PM ET
 
Session Chairs: Ingrid Pardo (Biogen)
 

10:00 AM

Session Overview

Chair

10:15 AM

Validation of Fluid-Based Neurobiomarkers in Nonclinical Toxicology Species

Madhu Sirivelu (Pfizer)

10:35 AM

Fluid-based Biomarkers of Neurotoxicity with Gene Therapy Toxicology Studies in NHPs

Kelly Penraat (Novartis)

11:05 AM

Safety Biomarkers of Peripheral Neurotoxicity in the Rat: (IMI, NeuroDeRisk Project)

Diethilde Theil (Novartis)

11:35 AM

Neurofilament to Monitor ALS and MS

Danielle Graham (Biogen)

12:05 PM

Panel Discussion/Q&A

12:35 PM

Break

Oct 11
Session 6: Biologics, Part II
October 11, 2022 ・ 1:00PM - 12:45PM ET
 
Session Chairs: Katy Fraser (Takeda), Maggie Willer (Takeda), Smita Salian-Mehta (Gilead)
 

1:00 PM

Session Overview

Chairs

1:05 PM

Contribution of 3-month Toxicology Studies to the Safety Assessment of ICH S9-Directed Bispecific T Cell Engagers

Petra Lutterbeuse (Amgen)

1:25 PM

De-Risking Liver Toxicity for a Biologic Modality

Nichole Vansell (Pfizer)

1:55 PM

Case Studies Assessing the Immunogenicity Risk of Host Cell Proteins in Antibody Biotherapeutics

Jeanine Bussiere (Amgen)

2:25 PM

Intravesical Delivery for an ADC Therapeutic

Chris Carosino (Seagen)

Day 5
Morning Networking Session @ 9:30AM ET
Oct 13
Session 7: Cell and Gene Therapy
October 13, 2022 ・ 10:00AM - 2:15PM ET
 
Session Chairs: Payal Rana (Pfizer) and Tynisha Glover (Janssen)
 

10:00 AM

Session Overview

Chairs

10:05 AM

Measuring Integration of Gene Therapy AAV Vectors into the Host Genome

Tom Lanz (Pfizer)

10:35 AM

Ocular Safety Associated with AAV Gene Therapy

Nick Buss (Kriya)

11:05 AM

Regulatory Considerations for the Nonclinical Safety Assessment of Gene Therapies

Jeff Moffit (Carbon Bio)

11:35 AM

PK Considerations in Gene Therapy

Nancy Chen (Takeda)

12:05 PM

Break

12:20 PM

Product Quality Issues for Cell and Gene Therapy Products

Sheri Nidositko (Novartis)

12:50 PM

Root-Cause Investigation of Nonclinical Human T Cell Lymphoma to Enable CTN Filing

Lauren Gauthier (Takeda)

1:50 PM

CAR T Consortium on Cytokine Independent Growth Assay

Shon Greene (Umoja Biopharma)